Natural History Data
Natural history studies are essential for understanding how CHM progresses and for designing effective clinical trials.
CRF partnered with the Rare Disease Cures Accelerator–Data and Analytics Platform (RDCA-DAP) to make CHM natural history data available to researchers worldwide. Two key datasets now available include:
- Efficacy and Safety of BIIB111 for the Treatment of Choroideremia (STAR)
- Sponsor: Biogen
- NCT: NCT03496012
- A Study to Assess Choroideremia (CHM) Health Outcomes
- Sponsor: Biogen
- NCT: NCT04750785
- Natural History of the Progression of Choroideremia Study
- Sponsor: Biogen (NightstaRx)
- NCP: NCT03359551
- Natural Disease Progression in Participants With Choroideremia
- NCP: NCT04795206
To access this data, create an account: RDCA-DAP Portal
More information about this collaborative effort can be found here:
CRF is registered as a US 501(c)3 nonprofit organization EIN: 04-3511754
Our mission is to raise funds in support of scientific research leading to a treatment or cure of choroideremia, a hereditary retinal-degenerative disease that causes blindness; to educate people affected by the disease; and to inform the public.
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